- Long-term Survival Benefit of Eculizumab Treatment in Patients With Paroxysmal Nocturnal Haemoglobinuria: Data From the International PNH Registry (2022)
- Different clinical characteristics of paroxysmal nocturnal hemoglobinuria in pediatric and adult patients (2016)
- Baseline characteristics and disease burden in patients in the International Paroxysmal Nocturnal Hemoglobinuria Registry (2014)
- Use of Blood Transfusions In Paroxysmal Nocturnal Hemoglobinuria Patients with and without Aplastic Anemia Enrolled In the Global PNH Registry (2010)
- Use of Blood Transfusions In Paroxysmal Nocturnal Hemoglobinuria Patients with and without Aplastic Anemia Enrolled In the Global PNH Registry (2010)