Goals – what we aim to have achieved

  1. Increase resilience of PNH patients
  2. Advocate on behalf of PNH patients to overcome practical, lifestyle challenges – helping them to live their lives to its full potential
  3. Utilise our knowledge of PNH patients’ experiences to shape and inform PNH care, treatment and research

Objectives – how we will go about achieving this

  1. Increase resilience of PNH patients
    • Ensure sustainable access to PNH-specialised psychological / emotional wellbeing for PNH patients at any point in their journey
    • Increase the quantity and variety of information available for PNH patients and their supporter
    • Further segment/stratify peer support so that PNH patients can speak to people with similar experiences – in particular, creating support for younger people
  2. Advocate on behalf of PNH patients to overcome practical, lifestyle challenges – helping them to live their lives to its full potential
    • Develop a clear understanding of the biggest barriers and unmet needs for PNH patients, and prioritise areas of focus for advocacy
    • Develop and deliver campaigns to address unmet needs, and overcome these barriers and challenges
  3. Utilise our knowledge of PNH patients’ experiences to shape and inform PNH care, treatment and research
    • Gather real world data on, and increase awareness of, the wide-ranging experience of living with PNH
    • Campaign for more, and increase patient involvement in, research into areas identified as priorities
    • Campaign to improve care in areas identified by patients and other experts
    • Engage and inform licensing and regulatory processes, e.g. NICE, MHRA

Enablers – what we know we need as an organisation in order to achieve our goals

  • Listen to and involve people living with PNH to shape everything we do
  • Recruit, support and retain excellent people as staff and volunteers
  • Increase our financial sustainability (broader funding mix – individuals, grants, earned income etc)
  • Build strong governance (including trustee recruitment, governance structure in addition to board)
  • Collect and use data to measure our impact, build our evidence base and shape our future work