Now in its second edition, The Guide to Living Well with PNH contains patient quotes, expert tips, and tools to help patients and caregivers not only better manage this condition, […]
New research study investigating how care should be co-ordinated for rare conditions Are you 18 or over and a patient with a rare or undiagnosed condition? Are you the parent […]
A recently published article on treating Aplastic Anaemia and PNH at the same time:…”aplastic anemia treatment decisions should not be influenced by the presence of PNH” Read more here.
This is the sub cutaneous daily injection which inhibits the C3 part of the complement system (rather than C5) and is promising for those who still need blood transfusions whilst […]
“Achillion Pharmaceuticals, Inc. announced (10 July) that the Company had begun dosing healthy volunteer subjects in a first-in-human phase 1 trial of ACH-5548, an oral small-molecule complement factor D inhibitor. ACH-5548 […]
